Abstract

Summary

This thesis investigates the molecular basis of melanopsin-driven light sensitivity by silencing OPN4 in rod/cone-deficient mice, establishing a reproducible in vivo model using pupillometry as a functional readout. The work has implications for future therapies aimed at restoring residual light sensitivity in blind patients by leveraging or augmenting the ipRGC/melanopsin pathway.
Abstract

Key Findings

  • siRNA-mediated knockdown achieved >85% silencing of melanopsin (OPN4) protein in Neuro2A cells as confirmed by immunolabelling.
  • Intravitreal siRNA injection in rd and rd/rd cl mice inhibited pupil light responses in vivo, functionally confirming Opn4 silencing detected by RT-PCR and molecular analysis.
  • The study established a novel reproducible in vivo model linking siRNA-induced melanopsin pathway silencing to measurable pupillometric and molecular endpoints across multiple timepoints.
Categories

Categories

The Science of Light: Investigates the molecular mechanisms of melanopsin (OPN4)-mediated phototransduction using siRNA knockdown in mouse models, directly probing ipRGC photoreceptor biology.
Eye Health & Vision: Explores therapeutic potential of OPN4 ectopic expression for restoring light sensitivity in degenerate retinas with complete photoreceptor loss.
Authors

Author(s)

AN Vachtsevanos
Publication Date

Publication Year

2012
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